Molecular Biology
Lesson 4 of 4 10 min +90 XP

CRISPR & Genome Editing

Rewriting DNA with molecular scissors.

What you'll learn

  • Explain how CRISPR-Cas9 targets DNA
  • Describe what the cut enables
  • Weigh a key ethical consideration
Find-and-replace for genes

A word processor lets you jump to an exact word and swap it. CRISPR gives biologists that find-and-replace power on DNA — guiding molecular scissors to one precise spot in a genome to cut and edit a single gene.

Programmable editing of the genome

CRISPR-Cas9 lets scientists edit DNA at a chosen location. A short guide RNA is designed to match a target sequence; it leads the Cas9 enzyme there, which cuts both strands. The cell's repair machinery then either disables the gene or, given a template, pastes in a new sequence.

Guide RNA = the address

The specificity comes from the guide RNA's base-pairing with the target DNA. Change the guide's sequence and you retarget the whole system — which is what makes CRISPR so flexible.

CRISPR is being used to develop therapies for sickle-cell disease and to engineer disease-resistant crops.
Ethics of germline editing

Editing somatic cells affects one patient; editing germline (embryos, eggs, sperm) changes all future descendants and raises serious ethical questions the field treats with great caution.

Lab · Retarget the tool
  1. You want Cas9 to cut a different gene.
  2. Identify which component determines where it cuts.
  3. State what you would change.

What you should see: The guide RNA determines the target, so you redesign the guide RNA to match the new gene's sequence.

Knowledge Check

+25 XP / correct

1. In CRISPR-Cas9, what determines the DNA location that gets cut?

2. Germline editing is ethically weighty because it…